P2 Economic Evaluation of Exagamglogene Autotemcel (EXA-CEL) Gene-Edited Therapy in Patients with Transfusion-Dependent Beta-Thalassemia
Abstract
Authors
C. Udeze H. Fang F.J. Ogunsile U. Mujumdar X. Nie H. Yang S. Jeyakumar N. Li J. Zhao A. Lopez