Mission
By identifying key challenges in assessing the value of innovative therapies, including advanced, emerging, and orphan* therapies, we aim to advance research and policy dialogue to support informed healthcare decision-making and foster equitable access for all patients.
*Includes treatments for rare diseases with and without regulatory orphan drug designation.
Goal
- Leadership – Lead HEOR community in issues on value assessments of emerging and orphan therapies and contribute to the relevant active consultations.
- Research – Identify priority topics, conduct research, and provide a platform for membership to engage on key projects that contribute to advance decision-making approaches for emerging and orphan therapies.
- Education – Facilitate educational exchange with membership on the latest HEOR trends and policy topics pertaining to emerging and orphan therapies.
Manuscripts & Reports
- Zimmermann, B, Spinner, D. S, Snyder, S.R, Purser, M. Can We Demonstrate the Value of Next-Generation Sequencing Approaches Within Traditional Value Frameworks? Value and Outcomes Spotlight. 2021; 7(5)
- Challenges in Research and Health Technology Assessment of Rare Disease Technologies Disease Terminology and Definitions—A Systematic Global Review
Leadership
Chairs
Ka Keat Lim, MSc, RPh, PhD
Carina Righetti, MSc, BSc
Past Chair
Joel Iff, PharmD, PhD
Renske ten Ham, PharmD
Melanie Whittington, MS, PhD
Working Groups
Key Project
In development
Member Engagement
These activities allow for a variety of members to participate and facilitates disseminating content in webinars, journal clubs, conference sessions and meetings, and online communities.
The Emerging and Orphan Therapies Online Community offers active ISPOR members a platform to engage in discussions, share resources, exchange experiences, and stay informed on SIG-related topics and updates. Join the ISPOR Emerging and Orphan Therapies Special Interest Group and connect with the online community today! Not yet an ISPOR member? Join today!
EMERGING AND ORPHAN THERAPIES ONLINE COMMUNITY - FOR MEMBERSQuestions or ideas? Please send an email to orphantherapiesSIG@ispor.org.