CO122 Late-Onset Pompe Disease (LOPD) Patients Treated with Avalglucosidase Alfa Show Favorable Results Compared to Cipaglucosidase Alfa Plus Miglustat: Indirect Treatment Comparison
Abstract
Authors
M. Roberts I. Proskorovsky P. Guyot P. Shukla M. Periquet N. Thibault A. Hamed L. Riou França L. Pollissard