PCR70 Avalglucosidase Alfa (AVA) Improves Symptoms and Functioning in Late-Onset Pompe Disease (LOPD) Patients vs Alglucosidase Alfa (ALG): Post-Hoc Analyses of Patient-Reported Outcomes (PROs) From COMET Trial
Abstract
Authors
A Toscano AT van der Ploeg KI Berger MM Dimachkie B Schoser C Gwaltney J Msihid A Hamed N Thibault L Pollissard PS Kishnani