PMU36 COST-UTILITY ANALYSIS OF SINGLE DOSE GENE-REPLACEMENT THERAPY FOR SPINAL MUSCULAR ATROPHY TYPE 1 COMPARED TO CHRONIC NUSINERSEN TREATMENT IN JAPAN
Abstract
Authors
R. Dean B. Miller R. Arjunji H. Awano A. Igarashi S. Tanaka D.E. Feltner D.M. Sproule I. Jensen O. Dabbous