PRO13 IMPACT OF CAREGIVER EXPERIENCE AND HRQOL IN LATER-ONSET SPINAL MUSCULAR ATROPHY (SMA): RESULTS FROM THE PHASE 3 CHERISH TRIAL
Abstract
Authors
S. Naoshy A.D. Paradis J. Montes N.B. Johnson D.C. Krasinski
S. Naoshy A.D. Paradis J. Montes N.B. Johnson D.C. Krasinski
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