PND18 THE RESTORE REGISTRY: A RESOURCE FOR MEASURING AND IMPROVING SPINAL MUSCULAR ATROPHY OUTCOMES
Abstract
Authors
D.C. De Vivo F. Khan R.S. Finkel P.B. Shieh E. Tizzano M. Droege J. Kirschner E. Mercuri F.A. Anderson F. Muntoni L. Servais O. Dabbous J.W. Day