PT7 Reassessment Dynamics of Orphan Drugs in Germany’s Benefit Assessment Process

PT8 Access to Orphan Medicines in Ireland

PT9 Drivers of Access to Gene Therapies in Poland and Selected Central and Eastern Europe Countries

PT10 Real-World Management of Patients With Immune Thrombocytopenia in Italy: A Retrospective Database Study

PT11 Authoring of Peer-Reviewed Articles on the Experiences of Patients With Rare Diseases by Patients and Their Caregivers: A Rapid Review

PT12 Perceptions of Rare Disease Patients and Their Caregivers Regarding Access to Disease Information and Interactions With Their Healthcare Providers: Results From an International Survey